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COMPLETED
NCT05514249
PHASE1
Treatment of a Single Patient With CRD-TMH-001
Sponsor: Cure Rare Disease, Inc
View on ClinicalTrials.gov
Summary
The study is a single patient study intended to understand the effects of a gene-editing therapeutic to treat a rare mutation of Duchenne muscular dystrophy.
Key Details
Gender
MALE
Age Range
18 Years - 28 Years
Study Type
INTERVENTIONAL
Enrollment
1
Start Date
2022-08-31
Completion Date
2022-10-12
Last Updated
2026-10-20
Healthy Volunteers
No
Conditions
Interventions
DRUG
CRD-TMH-001
Participant will receive a single dose of CRD-TMH-001 administered via intravenous injection.
Locations (1)
UMass Chan Medical School
Worcester, Massachusetts, United States