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Vatiquinone Expanded Access Protocol
Sponsor: Medical University of South Carolina
Summary
The purpose of this study is to provide participants who successfully completed the study titled "An Open-label, Safety Study for Previously Treated Vatiquinone (PTC743) Subjects With Inherited Mitochondrial Disease" with liquid Vatiquinone through an intermediate patient population expanded access protocol.
Official title: Expanded Access Protocol for Vatiquinone in Previously Treated Patients With Inherited Mitochondrial Disease
Key Details
Gender
All
Age Range
1 Year - Any
Study Type
EXPANDED_ACCESS
Enrollment
Not specified
Start Date
Not specified
Completion Date
Not specified
Last Updated
2026-04-09
Healthy Volunteers
Not specified
Conditions
Interventions
Vatiquinone
Vatiquinone will be administered per dose and schedule specified in the arm description.